Alexandria Forbes, PhD, President and CEO Professor Michel Michaelides, BSc, MB BS, MD(Res), FRCOphth, FACS Professor of Ophthalmology & Consultant Ophthalmic Surgeon at UCL Institute of Ophthalmology and Moorfields Eye Hospital. AAV-AIPL1 for the Treatment of Leber Congenital Amaurosis 4 (LCA4) Retinal Dystrophy AAV-AIPL1 for treatment of LCA4 genetic blindness 2 • MeiraGTx's rAAV8.hRKp.AIPL1 delivers the wild-type human AIPL1 gene under control of a photoreceptor- specific rhodopsin kinase promoter, hRK. ...