Haemopoietic stem cell (HSC) gene therapy
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Orchard Therapeutics Awarded Innovation Passport Designation for OTL-201 in MPS-IIIA
Globenewswire· 2026-04-30 14:30AI 处理中...
LONDON, April 30, 2026 (GLOBE NEWSWIRE) -- Orchard Therapeutics, a Kyowa Kirin company, announced it has been granted Innovation Passport designation for OTL-201, an investigational haemopoietic stem cell (HSC) gene therapy in development for the treatment of mucopolysaccharidosis type IIIA (MPS-IIIA). The designation was awarded under the recently refreshed Innovative Licensing and Access Pathway (ILAP) in the UK, which provides a single integrated platform for sustained collaboration between developers, t ...